Grand Hyatt Hotel, New York City 2012 | November 28-30
Grand Hyatt Hotel, New York City 2012 | November 28-30
Grand Hyatt Hotel, New York City 2012 | November 28-30
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18<br />
INNOvATOR PREsENTATION<br />
INNOvATOR PREsENTATION<br />
1:45 PM – 2:10 PM UriS/JULLiArd<br />
DART Therapeutics<br />
DART Therapeutics, LLC is an innovative, new model biotech designed to address the challenges of drug<br />
development in pediatric rare diseases. DART is a partnership between patient foundations and industry<br />
professionals. It is funded by two patient associations in Duchenne Muscular Dystrophy (Charley’s Fund<br />
and Nash Avery), and is managed by a team of seasoned industry professionals. Since presenting at<br />
Partnering for Cures in 2010, DART has acquired numerous therapeutic assets, completed a biomarker<br />
validation study that will benefit the entire DMD community, and expanded the management team.<br />
The DART model is a promising new way to navigate the “valley of death.”<br />
Presented by:<br />
gene WilliaMs, Chairman and CEO, DART Therapeutics, LLC<br />
2:15 PM – 2:40 PM BrOAdwAy<br />
Life Raft Group: GIST Collaborative Tissue Bank<br />
Fresh, frozen tissue, which is difficult to come by, as it is collected at the time of surgery, is considered to<br />
be the standard for patient tissue study. Formalin-fixed, paraffin-embedded tissue is much easier to access<br />
and use for large-scale studies, but is limited as a model for research testing. The Life Raft Group utilizes<br />
both methods of tissue collection in order to get the most benefit from the tissue. The presenter will explain<br />
the tissue process in detail and how it is transformative, collaborative, and employs de-identified patient<br />
histories to further enhance research findings.<br />
Presented by:<br />
norMan J. scherzer, Executive Director, The Life Raft Group