R R - American Society of Gene & Cell Therapy
R R - American Society of Gene & Cell Therapy
R R - American Society of Gene & Cell Therapy
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The <strong>American</strong> <strong>Society</strong> <strong>of</strong> <strong>Gene</strong> <strong>Therapy</strong>’s<br />
2004<br />
7th Annual Meeting<br />
final program<br />
Friday, June 4<br />
SS311 - Cardiovascular: <strong>Cell</strong> and <strong>Gene</strong> <strong>Therapy</strong> for Heart<br />
Failure<br />
Room: Auditorium Room 1<br />
Chair<br />
Todd K. Rosengart, MD<br />
Speakers<br />
Todd K. Rosengart, MD - Combined <strong>Gene</strong> and <strong>Cell</strong><br />
<strong>Therapy</strong> fro Treating Heart Disease<br />
Barry J. Byrne, MD, PhD - Approaches to Cardiac<br />
Hypertrophy Using AAV Vectors<br />
Frank J. Giordano, MD - <strong>Gene</strong> Regulation by Engineered<br />
Transcription Factor to Augment Cardiac Function<br />
SS312 - Embryonic Stem <strong>Cell</strong>s & Tissue Engineering<br />
Room: 205 A-D<br />
Chair<br />
Mervin Yoder, MD<br />
Speakers<br />
George Q. Daley, MD, PhD - Modeling Hematopoietic<br />
Transplantation with ES <strong>Cell</strong>s<br />
Lorenz Studer, MD - Human Embryonic Stem <strong>Cell</strong>s and<br />
Therapeutic Cloning in Neural Disease<br />
Jennifer L. West, PhD - Biomimetic Strategies in<br />
Vascular Tissue Engineering<br />
SS313 - <strong>Gene</strong>tic Diseases: <strong>Gene</strong> <strong>Therapy</strong> for <strong>Gene</strong>tic<br />
Disease Using Non-Replacement Strategies<br />
Room: 208 A-D<br />
Chair<br />
Mark A. Kay, MD, PhD<br />
Speakers<br />
Dieter Gruenert, PhD - Sequence-Specific<br />
Modification <strong>of</strong> Genomic DNA with Fragments <strong>of</strong> DNA<br />
Beverly L. Davidson, PhD - RNAi for Dominant<br />
Neurogenetic Diseases<br />
Ronald G. Crystal, MD - Correction <strong>of</strong> <strong>Gene</strong>tic<br />
Disorders at the Pre-mRNA Level by Spliceosomemediated<br />
Trans-splicing<br />
Christopher Walsh, MD, PhD - RNA Trans-Splicing and<br />
<strong>Gene</strong>tic Correction<br />
SS314 - Musculo-Skeletal: New Approaches to <strong>Therapy</strong><br />
<strong>of</strong> Musculo-Skeletal Diseases<br />
Room: 211 A-D<br />
Chair<br />
Michael Themis, PhD<br />
Speakers<br />
David W. Russell, MD, PhD - Collagen <strong>Gene</strong> Targeting in<br />
Mesenchymal Stem <strong>Cell</strong>s from Individuals with<br />
Osteogenesis Imperfecta<br />
Michael Themis, PhD - The Fetal Approach: A Novel<br />
<strong>Therapy</strong> for the Treatment <strong>of</strong> Musculo-Skeletal Disease<br />
Josephine Nalbantoglu, PhD - Dystrophin <strong>Gene</strong> Transfer<br />
Terence A. Partridge, PhD - Production <strong>of</strong> Dystrophin<br />
Protein in the Muscles <strong>of</strong> the MDX Mouse Induced by<br />
Local and Systemic Injection <strong>of</strong> Antisense<br />
Oligonucleotides<br />
SS315 - Special: Young Investigators Symposium<br />
Room: 200<br />
Chair<br />
Malcolm Brenner, MD, PhD<br />
Speakers<br />
Michael A. Barry, PhD - <strong>Cell</strong>-Targeting Technologies for<br />
<strong>Gene</strong> <strong>Therapy</strong><br />
Introduced by Arthur Beaudet, MD<br />
Laurence JN Cooper, MD, PhD - T-<strong>Cell</strong> <strong>Therapy</strong> for<br />
Malignant B <strong>Cell</strong>s<br />
Introduced by John Zaia, MD<br />
Matthew Weitzman, PhD - Lessons from the<br />
Battleground <strong>of</strong> Virus - Host Interactions<br />
Introduced by Inder Verma, PhD<br />
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