World Journal of Gastrointestinal Pathophysiology
World Journal of Gastrointestinal Pathophysiology
World Journal of Gastrointestinal Pathophysiology
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3 L<strong>of</strong>tus EV, Sandborn WJ. Epidemiology <strong>of</strong> inflammatory<br />
bowel disease. Gastroenterol Clin North Am 2002; 31: 1-20<br />
4 Baumgart DC, Carding SR. Inflammatory bowel disease:<br />
cause and immunobiology. Lancet 2007; 369: 1627-1640<br />
5 Abraham C, Cho JH. Inflammatory bowel disease. N Engl J<br />
Med 2009; 361: 2066-2078<br />
6 Kaser A, Zeissig S, Blumberg RS. Inflammatory bowel disease.<br />
Annu Rev Immunol 2010; 28: 573-621<br />
7 Waterman M, Xu W, Stempak JM, Milgrom R, Bernstein CN,<br />
Griffiths AM, Greenberg GR, Steinhart AH, Silverberg MS.<br />
Distinct and overlapping genetic loci in Crohn’s disease and<br />
ulcerative colitis: correlations with pathogenesis. Inflamm<br />
Bowel Dis 2011; 17: 1936-1942<br />
8 Baumgart DC, Sandborn WJ. Inflammatory bowel disease:<br />
clinical aspects and established and evolving therapies. Lancet<br />
2007; 369: 1641-1657<br />
9 Graff LA, Walker JR, Clara I, Lix L, Miller N, Rogala L, Rawsthorne<br />
P, Bernstein CN. Stress coping, distress, and health<br />
perceptions in inflammatory bowel disease and community<br />
controls. Am J Gastroenterol 2009; 104: 2959-2969<br />
10 Graff LA, Vincent N, Walker JR, Clara I, Carr R, Ediger J,<br />
Miller N, Rogala L, Rawsthorne P, Lix L, Bernstein CN. A<br />
population-based study <strong>of</strong> fatigue and sleep difficulties in<br />
inflammatory bowel disease. Inflamm Bowel Dis 2011; 17:<br />
1882-1889<br />
11 Lix LM, Graff LA, Walker JR, Clara I, Rawsthorne P, Rogala<br />
L, Miller N, Ediger J, Pretorius T, Bernstein CN. Longitudinal<br />
study <strong>of</strong> quality <strong>of</strong> life and psychological functioning for<br />
active, fluctuating, and inactive disease patterns in inflammatory<br />
bowel disease. Inflamm Bowel Dis 2008; 14: 1575-1584<br />
12 Cannom RR, Kaiser AM, Ault GT, Beart RW, Etzioni DA.<br />
Inflammatory bowel disease in the United States from 1998<br />
to 2005: has infliximab affected surgical rates? Am Surg 2009;<br />
75: 976-980<br />
13 Copelan EA. Hematopoietic stem-cell transplantation. N<br />
Engl J Med 2006; 354: 1813-1826<br />
14 Aiuti A, Bachoud-Lévi AC, Blesch A, Brenner MK, Cattaneo<br />
F, Chiocca EA, Gao G, High KA, Leen AM, Lemoine NR,<br />
McNeish IA, Meneguzzi G, Peschanski M, Roncarolo MG,<br />
Strayer DS, Tuszynski MH, Waxman DJ, Wilson JM. Progress<br />
and prospects: gene therapy clinical trials (part 2). Gene<br />
Ther 2007; 14: 1555-1563<br />
15 Alexander BL, Ali RR, Alton EW, Bainbridge JW, Braun<br />
S, Cheng SH, Flotte TR, Gaspar HB, Grez M, Griesenbach<br />
U, Kaplitt MG, Ott MG, Seger R, Simons M, Thrasher AJ,<br />
Thrasher AZ, Ylä-Herttuala S. Progress and prospects: gene<br />
therapy clinical trials (part 1). Gene Ther 2007; 14: 1439-1447<br />
16 Hunder NN, Wallen H, Cao J, Hendricks DW, Reilly JZ,<br />
Rodmyre R, Jungbluth A, Gnjatic S, Thompson JA, Yee C.<br />
Treatment <strong>of</strong> metastatic melanoma with autologous CD4+ T<br />
cells against NY-ESO-1. N Engl J Med 2008; 358: 2698-2703<br />
17 Garcia-Olmo D, Herreros D, Pascual I, Pascual JA, Del-Valle<br />
E, Zorrilla J, De-La-Quintana P, Garcia-Arranz M, Pascual<br />
M. Expanded adipose-derived stem cells for the treatment<br />
<strong>of</strong> complex perianal fistula: a phase II clinical trial. Dis Colon<br />
Rectum 2009; 52: 79-86<br />
18 Aiuti A, Cattaneo F, Galimberti S, Benningh<strong>of</strong>f U, Cassani B,<br />
Callegaro L, Scaramuzza S, Andolfi G, Mirolo M, Brigida I,<br />
Tabucchi A, Carlucci F, Eibl M, Aker M, Slavin S, Al-Mousa<br />
H, Al Ghonaium A, Ferster A, Duppenthaler A, Notarangelo<br />
L, Wintergerst U, Buckley RH, Bregni M, Marktel S, Valsecchi<br />
MG, Rossi P, Ciceri F, Miniero R, Bordignon C, Roncarolo<br />
MG. Gene therapy for immunodeficiency due to adenosine<br />
deaminase deficiency. N Engl J Med 2009; 360: 447-458<br />
19 Hacein-Bey-Abina S, Hauer J, Lim A, Picard C, Wang GP,<br />
Berry CC, Martinache C, Rieux-Laucat F, Latour S, Belohradsky<br />
BH, Leiva L, Sorensen R, Debré M, Casanova JL, Blanche<br />
S, Durandy A, Bushman FD, Fischer A, Cavazzana-Calvo M.<br />
Efficacy <strong>of</strong> gene therapy for X-linked severe combined immunodeficiency.<br />
N Engl J Med 2010; 363: 355-364<br />
WJGP|www.wjgnet.com<br />
van der Marel S et al . Emerging treatments for IBD<br />
20 Gaudet D, de Wal J, Tremblay K, Déry S, van Deventer S,<br />
Freidig A, Brisson D, Méthot J. Review <strong>of</strong> the clinical development<br />
<strong>of</strong> alipogene tiparvovec gene therapy for lipoprotein<br />
lipase deficiency. Atheroscler Suppl 2010; 11: 55-60<br />
21 Brunstein CG, Miller JS, Cao Q, McKenna DH, Hippen<br />
KL, Curtsinger J, Defor T, Levine BL, June CH, Rubinstein<br />
P, McGlave PB, Blazar BR, Wagner JE. Infusion <strong>of</strong> ex vivo<br />
expanded T regulatory cells in adults transplanted with umbilical<br />
cord blood: safety pr<strong>of</strong>ile and detection kinetics. Blood<br />
2011; 117: 1061-1070<br />
22 Duijvestein M, Vos AC, Roel<strong>of</strong>s H, Wildenberg ME, Wendrich<br />
BB, Verspaget HW, Kooy-Winkelaar EM, Koning F,<br />
Zwaginga JJ, Fidder HH, Verhaar AP, Fibbe WE, van den<br />
Brink GR, Hommes DW. Autologous bone marrow-derived<br />
mesenchymal stromal cell treatment for refractory luminal<br />
Crohn’s disease: results <strong>of</strong> a phase I study. Gut 2010; 59:<br />
1662-1669<br />
23 Ciccocioppo R, Bernardo ME, Sgarella A, Maccario R, Avanzini<br />
MA, Ubezio C, Minelli A, Alvisi C, Vanoli A, Calliada<br />
F, Dionigi P, Perotti C, Locatelli F, Corazza GR. Autologous<br />
bone marrow-derived mesenchymal stromal cells in the<br />
treatment <strong>of</strong> fistulising Crohn’s disease. Gut 2011; 60: 788-798<br />
24 Lau C, Soriano HE, Ledley FD, Finegold MJ, Wolfe JH,<br />
Birkenmeier EH, Henning SJ. Retroviral gene transfer into<br />
the intestinal epithelium. Hum Gene Ther 1995; 6: 1145-1151<br />
25 Lozier JN, Yankaskas JR, Ramsey WJ, Chen L, Berschneider<br />
H, Morgan RA. Gut epithelial cells as targets for gene therapy<br />
<strong>of</strong> hemophilia. Hum Gene Ther 1997; 8: 1481-1490<br />
26 Noel RA, Shukla P, Henning SJ. Optimization <strong>of</strong> gene transtransfer into intestinal epithelial cells using a retroviral vector. J<br />
Pediatr Gastroenterol Nutr 1994; 19: 43-49<br />
27 Matsumoto H, Kimura T, Haga K, Kasahara N, Anton P,<br />
McGowan I. Effective in vivo and ex vivo gene transfer to<br />
intestinal mucosa by VSV-G-pseudotyped lentiviral vectors.<br />
BMC Gastroenterol 2010; 10: 44<br />
28 Barbara G, Xing Z, Hogaboam CM, Gauldie J, Collins SM.<br />
Interleukin 10 gene transfer prevents experimental colitis in<br />
rats. Gut 2000; 46: 344-349<br />
29 Lindsay JO, Ciesielski CJ, Scheinin T, Hodgson HJ, Brennan<br />
FM. The prevention and treatment <strong>of</strong> murine colitis using<br />
gene therapy with adenoviral vectors encoding IL-10. J Immunol<br />
2001; 166: 7625-7633<br />
30 Lindsay J, Van Montfrans C, Brennan F, Van Deventer S,<br />
Drillenburg P, Hodgson H, Te Velde A, Sol Rodriguez Pena<br />
M. IL-10 gene therapy prevents TNBS-induced colitis. Gene<br />
Ther 2002; 9: 1715-1721<br />
31 Polyak S, Mah C, Porvasnik S, Herlihy JD, Campbell-<br />
Thompson M, Byrne BJ, Valentine JF. Gene delivery to intestinal<br />
epithelial cells in vitro and in vivo with recombinant<br />
adeno-associated virus types 1, 2 and 5. Dig Dis Sci 2008; 53:<br />
1261-1270<br />
32 During MJ, Xu R, Young D, Kaplitt MG, Sherwin RS, Leone<br />
P. Peroral gene therapy <strong>of</strong> lactose intolerance using an<br />
adeno-associated virus vector. Nat Med 1998; 4: 1131-1135<br />
33 O’Neill MJ, Bourre L, Melgar S, O’Driscoll CM. Intestinal<br />
delivery <strong>of</strong> non-viral gene therapeutics: physiological barriers<br />
and preclinical models. Drug Discov Today 2011; 16:<br />
203-218<br />
34 Blaese RM, Culver KW, Chang L, Anderson WF, Mullen C,<br />
Nienhuis A, Carter C, Dunbar C, Leitman S, Berger M. Treatment<br />
<strong>of</strong> severe combined immunodeficiency disease (SCID)<br />
due to adenosine deaminase deficiency with CD34+ selected<br />
autologous peripheral blood cells transduced with a human<br />
ADA gene. Amendment to clinical research project, Project<br />
90-C-195, January 10, 1992. Hum Gene Ther 1993; 4: 521-527<br />
35 Culver KW, Osborne WR, Miller AD, Fleisher TA, Berger M,<br />
Anderson WF, Blaese RM. Correction <strong>of</strong> ADA deficiency in<br />
human T lymphocytes using retroviral-mediated gene transfer.<br />
Transplant Proc 1991; 23: 170-171<br />
36 Anderson WF, Blaese RM, Culver K. The ADA human gene<br />
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