Pompe's disease - RePub - Erasmus Universiteit Rotterdam

3
Long Term Intravenous Treatment of
Pompe’s Disease With Recombinant
Human Alpha Glucosidase From Milk
Hannerieke M.P. Van den Hout MD PhD 1 , Joep H.J. Kamphoven MD 1,2 ,
Léon P.F. Winkel MD 1 , Willem F.M. Arts MD PhD 3 , Johannes B.C. De Klerk MD 1 ,
M.Christa B. Loonen MD PhD 3 , Arnold G. Vulto PharmD PhD 4 , Adri Cromme-Dijkhuis
MD PhD 5 , Nynke Weisglas-Kuperus 6 , Wim Hop PhD 7 , Hans Van Hirtum MSc 2 ,
Otto P. Van Diggelen PhD 2 , Marijke Boer MSc 2 , Marian A. Kroos MSc 2 ,
Pieter A. Van Doorn MD PhD 8 , Edwin Van der Voort MD 9 , Barbara Sibbles MD PhD 10 ,
Emiel J.J.M. Van Corven PhD 11 , Just P.J. Brakenhoff PhD 11 , Johan Van Hove MD PhD 12 ,
Jan A.M. Smeitink MD PhD 13 , Gerard de Jong MD PhD 14 , Arnold J.J. Reuser PhD 2 ,
Ans T. Van der Ploeg MD PhD 1*
1 Department of Pediatrics, Division of Metabolic Diseases and Genetics,
5 Division of Pediatric Cardiology, 6 Division of Neonatology, 9 Division of Pediatric Intensive Care,
10 Dept. of Pediatrics, 3 Department of Pediatric Neurology, Erasmus MC-Sophia, Rotterdam,
Dr. Molewaterplein 60, 3015 GJ, Rotterdam, The Netherlands.
2 Department of Clinical Genetics, 7 Department of Epidemiology and Biostatistics, Erasmus MC, Rotterdam,
Dr. Molewaterplein 50, 3015 GE Rotterdam, The Netherlands.
14 Department of Internal Medicine, 4 Hospital Pharmacy, 8 Department of Neurology, Erasmus MC, Rotterdam,
Dr. Molewaterplein 40, 3015 GD Rotterdam, The Netherlands.
11 Pharming-Genzyme LLC, Archimedesweg 4, 2333 CN, Leiden, The Netherlands.
12 Department of Pediatrics, University Hospital Gasthuisberg, Herestraat 49, B-3000 Leuven, Belgium.
13 Department of Pediatrics, Division of Metabolic Diseases, University Medical Center Nijmegen, Geert
Grooteplein 10, P O Box 9101, 6500 HB Nijmegen, The Netherlands.
-in press, Pediatrics 2004-