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Final Program in it's entirety - MyGirlsBlood

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Congress Sessions cont’d<br />

n Inhibitor Incidence <strong>in</strong> Hemophilia A Patients<br />

Intensively Treated with Cont<strong>in</strong>uous Infusion<br />

of Factor VIII<br />

Batorova A1 , Holme P2 , Gr<strong>in</strong>geri A3 , Fijnvandraat<br />

K4 , Richards M5 , Hermans C6 , Altisent C7 , Lopez-<br />

Fernández M8 on behalf of the European<br />

Hemophilia Treatment Standardization Board<br />

(EHTSB)<br />

1National Hemophilia Center, Dept. of<br />

Hematology and Transfusion Medic<strong>in</strong>e, University<br />

Hospital, Bratislava, Slovakia, 2Haematology Medical Department, Rikshospitalet, University<br />

Hospital, Oslo, Norway, 3Centro Emofilia A.<br />

Bianchi Bonomi, University Hospital, Milan, Italy,<br />

4Department of Pediatric Hematology, Academic<br />

Medical Center, Amsterdam, the Netherlands,<br />

5Paediatric Haematology Department, Children’s<br />

Day Hospital, St. James University Hospital,<br />

Leeds, United K<strong>in</strong>gdom, 6Haemostasis Department, Cl<strong>in</strong>iques Universitaires St Luc,<br />

Bruxelles, Belgium, 7Servicio de Hematologia –<br />

Unidad de Hemofilia, Hospital Val d’ Hebron,<br />

Barcelona, 8Thrombosis and Haemostasis Unit.<br />

Servicio de Hematología y Hemoterapia,<br />

Complexo Hospitalario Universitario de A<br />

Coruña, Coruña, Spa<strong>in</strong><br />

n Factor VIII Light Cha<strong>in</strong> Mutations and Cyste<strong>in</strong>e<br />

Substitutions Predispose for Inhibitor<br />

Development <strong>in</strong> Mild and Moderate<br />

Hemophilia A: First Results From the<br />

INSIGHT Study<br />

Eckhardt CL1 , 2 , Peters M1 , Kamphuisen PW2 ,<br />

Astermark J3 , Oldenburg J4 , Hay CRM5 ,<br />

Santagost<strong>in</strong>o E6 , Ingerslev J7 , D’Oiron R8 , van der<br />

Bom JG9 and Fijnvandraat K1 for the INSIGHT<br />

<strong>in</strong>vestigators<br />

1Paediatric Haematology, Emma Children’s<br />

Hospital, Amsterdam, the Netherlands, 2Vascular Medic<strong>in</strong>e, Academic Medical Center,<br />

Amsterdam, the Netherlands, 3Centre for<br />

Thrombosis and Haemostasis, Malmö University<br />

Hospital, Lund University, Malmö, Sweden,<br />

4Institute of Experimental Haematology and<br />

Transfusion Medic<strong>in</strong>e, University Hospital Bonn,<br />

Bonn, Germany, 5Hemophilia Center, Manchester<br />

Royal Infirmary, Manchester, U.K., 6Angelo Bianchi Bonomi Hemophilia and Thrombosis<br />

Center, IRCCS Maggiore Hospital, Mangiagalli &<br />

Reg<strong>in</strong>a Elena Foundation, University of Milan,<br />

Milan, Italy, 7University Hospital Skejby, Aarhus,<br />

Denmark, 8Haemophilia Centre, Hôpital Bicêtre,<br />

Paris, France, 9Cl<strong>in</strong>ical Epidemiology, Leiden<br />

University Medical Center, Leiden, the<br />

Netherlands<br />

n Inhibitor Incidence <strong>in</strong> Previously Untreated<br />

Patients (PUPs) with Hemophilia A and B -<br />

<strong>F<strong>in</strong>al</strong> Evaluation of the Prospective PUP Study<br />

Conducted by the Paediatric Committee of<br />

the GTH (German, Swiss, and Austrian Society<br />

of Thrombosis and Haemostasis Research)<br />

Kreuz W1 , Auerswald G2 , Budde U3 , Lenk H4 ,<br />

Escuriola Ett<strong>in</strong>gshausen C1, on behalf of GTH-<br />

PUP-Study-Group<br />

1JW Goethe University Hospital, Dept. Pediatrics<br />

III, Frankfurt, 2ZKH St.Jürgen-Straße, Prof. Hess<br />

Childrens Hospital, Bremen, 3AescuLaboratory, Hamburg, 4University Hospital Leipzig, Dept.<br />

Pediatrics, Germany<br />

n First Human Dose Trial of Subcutaneously<br />

Adm<strong>in</strong>istered Recomb<strong>in</strong>ant Activated Factor<br />

VII (rFVIIa) to Hemophilia A and B Patients<br />

Shows Prolonged FVIIa Half-Life, and Provides<br />

Evidence of Safety and Tolerability<br />

Tiede A1 , Lethagen S2 , Friedrich U3 , Stenmo C3 ,<br />

Allen G4 , Giangrande P5 , Goudemand J6 , Hay C7 ,<br />

Holmström M8 , Klamroth R9 , McKenzie S10 ,<br />

Miesbach W11 , Negrier C12 , Jimenez Yuste V13 and<br />

Berntorp E14 1Hannover Medical School, Hannover, Germany,<br />

2 3 Rigshospitalet, Copenhagen, Denmark, Novo<br />

Nordisk A/S, Bagsvaerd, Denmark, 4Children’s Memorial Hospital, Chicago, U.S.A., 5Churchill Hospital, Oxford, U.K., 6Hôpital Cardiologique,<br />

Lille Cedex, France, 7Manchester Royal Infirmary,<br />

Manchester, U.K., 8Karol<strong>in</strong>ska Universitetssjukhuset, Stockholm, Sweden,<br />

9Vivantes Kl<strong>in</strong>ikum im Friedrichsha<strong>in</strong>, Berl<strong>in</strong>,<br />

Germany, 10Thomas Jefferson University,<br />

Philadelphia, U.S.A., 11Institut für<br />

Transfusionsmediz<strong>in</strong> Universitätskl<strong>in</strong>ikum<br />

Frankfurt, Germany, 12Hôpital Edouard Herriot,<br />

Lyon, France, 13Hospital Universitario La Paz,<br />

Madrid, Spa<strong>in</strong>, 14Universitetssjukhuset MAS,<br />

Malmö, Sweden<br />

n Why Is the Frequency of Inhibitors Increas<strong>in</strong>g<br />

Among Swedish Children with Severe<br />

Hemophilia A?<br />

Ljung R1 , Petr<strong>in</strong>i P2 , Holmberg F1 1Lund University, Departments of Paediatrics and<br />

Malmö Centre for Thrombosis and Haemostasis,<br />

University Hospital, Malmö, Sweden and<br />

2Paediatric Department of Coagulation<br />

Disorders, Karol<strong>in</strong>ska University Hospital,<br />

Stockholm, Sweden<br />

35<br />

Wednesday, July 14. 2010

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