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Final Program in it's entirety - MyGirlsBlood

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Posters, Sunday and Monday<br />

Index of Poster Presenters cont’d<br />

07P12<br />

Pharmacok<strong>in</strong>etic, Efficacy and Safety Data of the First<br />

Recomb<strong>in</strong>ant Factor VIII from a Human Cell L<strong>in</strong>e<br />

Knaub S1 , Jansen M1 , Zozulya N2 , Plyushch O2 1 2 Octapharma AG, Hematology Scientific Center of Russian<br />

Academy of Medical Science, Lachen, Russia<br />

07P13<br />

A Prospective, Randomized, and Crossover Study of an<br />

Activated Prothromb<strong>in</strong> Complex Concentrate for Secondary<br />

Prophylaxis <strong>in</strong> Patients with Hemophilia A and Inhibitors (Pro-<br />

FEIBA): Subject Demographics and Safety Data<br />

Leiss<strong>in</strong>ger C1 , Négrier C2 , Berntorp E3 , W<strong>in</strong>dyga J4 , Serban<br />

M5 , Bülent A6 , Lassila R7 , Kavakli K8 , Zulfikar B9 , Gr<strong>in</strong>geri A10 1Louisiana Center For Bleed<strong>in</strong>g And Clott<strong>in</strong>g, Tulane<br />

University Medical Center, Tulane, France 2Hemophilia Treatment Center, Hôpital Edouard Herriot, University Claude<br />

Bernard, Lyon, France, 3Malmö University Hospital, Malmö<br />

Centre for Thrombosis and Hemostasis, Malmö, Sweden,<br />

4Institute of Hematology and Transfusion Medic<strong>in</strong>e, Warsaw,<br />

Poland, 5Emergency Cl<strong>in</strong>ic for Children, Timisoara, Romania,<br />

6 7 Çukurova University, Adana, Turkey, Division of Coagulation<br />

Disorders, Hels<strong>in</strong>ki University Central Hospital, Hels<strong>in</strong>ki,<br />

F<strong>in</strong>land, 8University of Ege, Izmir, Turkey, 9Istanbul University,<br />

10 Istanbul, Turkey, Bianchi Bonomi Hemophilia and<br />

Thrombosis Center, University of Milan, Milan, Italy<br />

07P14<br />

Phase I, Randomized, Double-Bl<strong>in</strong>d, Placebo-Controlled,<br />

S<strong>in</strong>gle-Dose Escalation Study of the rFVIIa Variant (BAY 86-<br />

6150) <strong>in</strong> Hemophilia A or B with or without Inhibitors<br />

Mahlangu J1 , Coetzee M2 , Laffan M3 , W<strong>in</strong>dyga J4 , Yee T5 ,<br />

Schroeder J6 1Hemophilia Comprehensive Care Center, Charlotte Maxeke<br />

Johannesburg Academic Hospital And University Of The<br />

Witwatersrand, 2Bloemfonte<strong>in</strong> Haemophilia Treatment<br />

Centre, University of the Free State, Bloemfonte<strong>in</strong>, South<br />

Africa, 3Imperial College, Hammersmith Hospital, London,<br />

U.K., 4Institute of Hematology and Transfusion Medic<strong>in</strong>e,<br />

Warsaw, Poland, 5The Royal Free Hospital, London, U.K.,<br />

6Bayer Scher<strong>in</strong>g Pharma AG, Berl<strong>in</strong>, Germany<br />

07P15<br />

Long-Term Cl<strong>in</strong>ical Safety of FEIBA, Activated Prothromb<strong>in</strong><br />

Complex Concentrate (APCC) <strong>in</strong> Japanese Inhibitor Subjects:<br />

An Update of Post-Authorization Safety Surveillance (PASS)<br />

<strong>Program</strong><br />

Midori S 1 , Kagehiro A2 , Ei K3 , Sh<strong>in</strong>ji M4 , Tadashi M5 , Satoshi<br />

H6 , Teruhisa F7 , Michio S8 and the FINE study group9 1 2 Nara Medical University, Nara Tokyo Medical University<br />

Hospital, 3Ogikubo Hospital, 4St. Marianna University School<br />

of Medic<strong>in</strong>e, Kanagawa, 5Nagoya University School of<br />

Medic<strong>in</strong>e, Aichi, 6Hyogo College of Medic<strong>in</strong>e, Hyogo,<br />

7 8 Hiroshima University Hospital, Hiroshima, University of<br />

Environmental and Occupational Health Japan, Fukuoka,<br />

and 9Baxter BioScience Japan, Medical Affairs Cl<strong>in</strong>ical Trial,<br />

Tokyo, Japan<br />

50<br />

07P16<br />

Long-Act<strong>in</strong>g Glycopegylated Recomb<strong>in</strong>ant Activated Factor<br />

VII (LA-rFVIIa) is Safe and Shows a Prolonged FVIIa Half-Life<br />

after S<strong>in</strong>gle and Multiple Adm<strong>in</strong>istrations <strong>in</strong> Hemophilia A<br />

and B Patients, Mak<strong>in</strong>g it Suitable for Development as<br />

Prophylactic Treatment of Patients with Hemophilia and<br />

Inhibitors<br />

Møss J1 , Stenmo C1 , Jimenez-Yuste V2 , Bottcher S1 ,<br />

Fernandez, I2 1 2 Novo Nordisk A/S, Denmark, Hospital Universitario La Paz,<br />

Madrid, Spa<strong>in</strong><br />

07P17<br />

Efficacy, Safety and Immunogenicity of Wilate ® <strong>in</strong> Children<br />

Under 6 Years of Age with Inherited von Willebrand Disease<br />

Nowak-Goettl U1 , Kruempel A1 , Russo A2 , Jansen M3 , Knaub S4 1University Hospital, Westfälische Wilhelms-Universität,<br />

Münster, Germany, 2University Hospital, Johannes Gutenberg-<br />

3 Universität Ma<strong>in</strong>z, Germany, Octapharma Produk -<br />

tionsgesellschaft mbH, Vienna, Austria, 4Octapharma AG,<br />

Lachen, Switzerland<br />

07P18<br />

Safety and Efficacy of B-Doma<strong>in</strong>-Deleted Recomb<strong>in</strong>ant FVIII<br />

– <strong>F<strong>in</strong>al</strong> Results of a 10-Year Pharmacovigiliance Study<br />

Westfeld M1 , Pollmann H2 for the ReFacto ® Phar -<br />

macovigilance Data Monitor<strong>in</strong>g Board<br />

1Wyeth Pharma GmbH - e<strong>in</strong> Unternehmen der Pfizer-Gruppe,<br />

2 Muenster, ITH - Institut für Thrombophilie und<br />

Haemostaseologie, Bonn, Germany<br />

07P19<br />

Two-year Interim Results of a Non-Interventional Trial to<br />

Assess the Safety and Efficacy of Treatment with<br />

Recomb<strong>in</strong>ant Factor IX<br />

Westfeld M1 , Pollmann H2 , Oldenburg J3 1Wyeth Pharma GmbH - e<strong>in</strong> Unternehmen der Pfizer-Gruppe,<br />

2 Muenster, ITH - Institut für Thrombophilie und<br />

Haemostaseologie, 3Universitaetskl<strong>in</strong>ikum Bonn, Germany<br />

07P20<br />

Cl<strong>in</strong>ical Efficacy of a Novel VWF-Conta<strong>in</strong><strong>in</strong>g FVIII<br />

Concentrate, Wilate ® , <strong>in</strong> the Prophylaxis and Treatment of<br />

Bleed<strong>in</strong>g Episodes <strong>in</strong> Previously Treated Hemophilia A<br />

Patients<br />

Klukowska A1 , W<strong>in</strong>dyga J2 , Batorova A3 1Department of Pediatrics, Hematology and Oncology,<br />

Medical University of Warsaw, Warszawa, Poland,<br />

2Department of Hemostasis Disturbances and Internal<br />

Diseases, Institute of Hematology and Transfusiology,<br />

Warszawa, Poland, 3University Hospital Cl<strong>in</strong>ic Haematology<br />

& Blood Transfusion, Bratislava, Slovak Republic

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