FINAL PROGR AM - American Society of Gene & Cell Therapy
FINAL PROGR AM - American Society of Gene & Cell Therapy
FINAL PROGR AM - American Society of Gene & Cell Therapy
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<strong>AM</strong>ERICAN SOCIETY OF GENE THERAPY • Final Program 35<br />
SCIENTIFIC <strong>PROGR</strong><strong>AM</strong><br />
FRIDAY, JUNE 3, 2005<br />
Scientific Symposium 303<br />
Infectious Disease: <strong>Gene</strong> <strong>Therapy</strong> for HIV: Lessons<br />
Learned, Paradigms to Apply to Other Areas<br />
Room: 260/264<br />
Co-Chairs: Boro Dropulic, PhD<br />
Ramesh Akkina, DVM, PhD<br />
Speakers: Dale Ando, MD - <strong>Gene</strong> Modulation <strong>of</strong> the HIV<br />
Co-receptor CCR5 Using CCR5 Specific Zinc<br />
Finger Nucleases<br />
Dorothee Von Laer, MD - Treatment <strong>of</strong> HIV<br />
Infection with <strong>Gene</strong> Protected Autologous T cells<br />
Carl H. June, MD - Lentiviral <strong>Gene</strong> <strong>Therapy</strong> for<br />
HIV: A New Paradigm?<br />
John J. Rossi, PhD - RNAi <strong>Gene</strong> <strong>Therapy</strong> for<br />
HIV-1<br />
Scientific Symposium 304<br />
Musculo-Skeletal: Regenerative Approaches for Skeletal<br />
Disorders<br />
Room: 263/267<br />
Chair: Steven C. Ghivizzani, PhD<br />
Speakers: Christopher Evans, PhD - Tissue Regeneration<br />
Without Manufactured Scaffolds or <strong>Cell</strong> Culture<br />
Dan Gazit, DMD, PhD - <strong>Gene</strong>tically<br />
Engineered Mesenchymal Stem <strong>Cell</strong>s as a Platform<br />
for Skeletal Tissue Engineering<br />
Paul D. Robbins, PhD - <strong>Gene</strong> <strong>Therapy</strong> for Bone<br />
and Cartilage Regeneration<br />
Edward M. Schwarz, PhD - Revitalization <strong>of</strong><br />
Structural Allografts via Immobilized rAAV <strong>Gene</strong><br />
<strong>Therapy</strong><br />
BREAK – 10:00 <strong>AM</strong> - 10:15 <strong>AM</strong><br />
SCIENTIFIC SYMPOSIA – 10:15 <strong>AM</strong> - 12:15 PM<br />
Scientific Symposium 310<br />
Embryonic Stem <strong>Cell</strong>s and Tissue Engineering<br />
Room: 230 Complex<br />
Chair: Carolyn Lutzko, PhD<br />
Speakers: Linda G. Griffith, PhD - Microscale Models <strong>of</strong><br />
Liver for Analysis <strong>of</strong> <strong>Gene</strong> <strong>Therapy</strong><br />
Mervin Yoder, MD - Using RNA Interference<br />
Approaches to Modulate <strong>Gene</strong> Expression in ES<br />
<strong>Cell</strong>s<br />
Kyunghee Choi, PhD - Stepwise Commitment<br />
from Embryonic Stem to Hematopoietic and<br />
Endothelial <strong>Cell</strong>s<br />
Michael R. Linden, PhD - AAV-mediated Site-<br />
Specific <strong>Gene</strong> Addition in Embryonic Stem <strong>Cell</strong>s<br />
Scientific Symposium 311<br />
Immunology <strong>of</strong> <strong>Gene</strong> <strong>Therapy</strong>: Immune Response to<br />
<strong>Gene</strong> Transfer Vehicles<br />
Room: 240 Complex<br />
Chair: Hildegund CJ Ertl, MD<br />
Speakers: James M. Wilson, MD, PhD - T <strong>Cell</strong><br />
Responses to Adenoviruses and AAV<br />
Katherine A. High, MD - Immune Responses to<br />
Vector and Transgene Product in AAV-mediated<br />
<strong>Gene</strong> Transfer<br />
Thierry C. Vandendriessche, PhD -<br />
Transduction <strong>of</strong> Antigen-Presenting <strong>Cell</strong>s using<br />
Viral Vectors: A Double Edged Sword<br />
Scientific Symposium 312<br />
Neural Disorders: Inherited Metabolic Brain Disorders<br />
Room: Ferrara Theater<br />
Chair: Beverly L. Davidson, PhD<br />
Speakers: Luigi Naldini, MD, PhD - HSC-based <strong>Gene</strong><br />
<strong>Therapy</strong> <strong>of</strong> Leukodystrophies<br />
John H. Wolfe, VMD, PhD - <strong>Gene</strong> <strong>Therapy</strong> for<br />
the CNS in Lysosomal Storage Disease<br />
Paola Leone, PhD - Safety and Efficacy <strong>of</strong><br />
AAV-mediated <strong>Gene</strong> Transfer for Canavan Disease<br />
Ronald G. Crystal, MD - AAV-mediated <strong>Gene</strong><br />
Transfer for Batten Disease<br />
Scientific Symposium 313<br />
Nonviral: Nonviral <strong>Gene</strong> Delivery: Towards Clinical<br />
Applications<br />
Room: 260/264<br />
Chair: Dexi Liu, PhD<br />
Speakers: Lluis M. Mir, DSc - Electric Pulses-based <strong>Gene</strong><br />
Transfer: Safety and Efficacy <strong>of</strong> Combinations <strong>of</strong><br />
High Voltage and Low Voltage Pulses<br />
Hans J. Lipps, PhD - A Novel Non-viral<br />
Episomal Vector as Expression System for <strong>Gene</strong><br />
<strong>Therapy</strong><br />
Michael A. Barry, PhD - Endonucleases as<br />
Barriers to <strong>Gene</strong> Delivery<br />
William M. Pardridge, MD - Intravenous,<br />
Non-Viral <strong>Gene</strong> <strong>Therapy</strong> <strong>of</strong> Brain in Rodents and<br />
Primates