Final Program - American Society of Gene & Cell Therapy
Final Program - American Society of Gene & Cell Therapy
Final Program - American Society of Gene & Cell Therapy
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Abstract Directory, Thursday, May 16, 2013<br />
Poster Session I, continued<br />
4:00 PM - 6:00 PM<br />
Room: Exhibit Hall C/D<br />
<strong>Gene</strong> Regulation<br />
233<br />
Lentiviral Vector-Based Insertional Mutagenesis<br />
Identiies New Oncogenes and Molecular Networks<br />
That Control Hepatocyte Transformation and<br />
Metabolism<br />
Marco Ranzani, Daniela Cesana, Cynthia Bartholomae, Francesca<br />
Sanvito, Stefano Annunziato, Michela Riba, Fabrizio Benedicenti,<br />
Pierangela Gallina, Claudio Doglioni, Christ<strong>of</strong> von Kalle, Yoon Jun<br />
Kim, Elia Stupka, Manfred Schmidt, Giovanni Tonon, Luigi Naldini,<br />
Eugenio Montini.<br />
240<br />
Spacio-Temporal Mutagenesis in Muscle by Using AAV-<br />
Cre Vectors: The Example <strong>of</strong> the Mtm1 <strong>Gene</strong><br />
Romain Joubert, Alban Vignaud, Mickaël Le, Christelle Moal, Nadia<br />
Messaddeq, Anna Buj-Bello.<br />
241<br />
Synergistic and Tunable <strong>Gene</strong> Activation by<br />
Combinations <strong>of</strong> Synthetic Transcription Factors<br />
Pablo Perez-Pinera, David G. Ousterout, Jonathan M. Brunger,<br />
Alicia M. Farin, Katherine A. Glass, Farshid Guilak, Gregory E.<br />
Crawford, Alexander J. Hartemink, Charles A. Gersbach.<br />
242<br />
A Novel Enhancer Increases the Level and Duration <strong>of</strong><br />
Transgene Expression in Mice<br />
Chunbo Zhang, Leping Li, Dexi Liu.<br />
Thursday, May 16, 2013<br />
234<br />
Detection <strong>of</strong> RNA Interference (RNAi) Mediated mRNA<br />
Cleavage in Fresh Injected Tumor Tissue from Patients<br />
a Phase I Trial <strong>of</strong> an Intratumoral pbi-shRNA Lipoplex<br />
Targeting Stathmin-1<br />
Zhaohui Wang, Donald D. Rao, Phillip B. Maples, Neil Senzer, John<br />
Nemunaitis.<br />
235<br />
LncRNA Saf Interacts with SPF45 To Promote Fas<br />
Receptor Alternative Splicing in Maturing Erythroid<br />
<strong>Cell</strong>s<br />
Olga Villamizar, Christopher B. Chambers, Janice M. Riberdy, Derek<br />
A. Persons, Andrew Wilber.<br />
236<br />
Stable and Selective Production <strong>of</strong> Therapeutic Protein<br />
in the Breastmilk <strong>of</strong> Non-Transgenic Mice Via Early<br />
Gestational Intra-Amniotic <strong>Gene</strong> Transfer<br />
Jesse D. Vrecenak, Miroslaw Kozlowski, Carlyn A. Todorow,<br />
Antoneta Radu, Alan W. Flake.<br />
237<br />
Improved Engraftment <strong>of</strong> Lentivirally Transduced<br />
Adipose Tissue-Derived Stem <strong>Cell</strong>s for Hemophilia B<br />
<strong>Therapy</strong> Using Bioengineered <strong>Cell</strong> Sheet Technology<br />
Inkyong Shim, Kazuo Ohashi, Kohei Tatsumi, Natsumi Watanabe,<br />
Yuji Kashiwakura, Tsukasa Ohmori, Yoichi Sakata, Makoto Inoue,<br />
Mamoru Hasegawa, Teruo Okano.<br />
238<br />
Targeted PLGA Nanoparticles Encapsulating Histone<br />
Deacetylase Inhibitor, Panobinostat Effectively Control<br />
T <strong>Cell</strong> Leukemia<br />
Boyoung Choi, Jangwook Lee, Jeong-A. Shin, Dahye Lee, Kuen Yong<br />
Lee, Priti Kumar, Sang-Kyung Lee.<br />
239<br />
Radiosensitivity <strong>of</strong> Human Induced Pluripotent Stem<br />
<strong>Cell</strong>s (hiPSC) Detectable by <strong>Cell</strong> Cycle Analysis<br />
Frank Houghton, Michael W. Epperly, Xichen Zhang, Vishwajit<br />
Nimgaonkar, Joel S. Greenberger.<br />
243<br />
Design and Screening <strong>of</strong> Custom Zinc Finger<br />
Transcription Factors To Modulate Expression <strong>of</strong> <strong>Gene</strong>s<br />
Controlling <strong>Cell</strong> Fate<br />
Ashley L. Fischer, Qingzhou Ji, Erik R. Eastlund, Mark A. Gerber,<br />
Carol A. Kreader, Scott W. Knight.<br />
244<br />
TaqMan® Assays for Assessment <strong>of</strong> Genome,<br />
Epigenome and Quality <strong>of</strong> Pluripotent Stem <strong>Cell</strong>s<br />
Andrew Fontes, Rene H. Quintanilla, Jeffrey Fergus, Uma<br />
Lakshmipathy.<br />
245<br />
An ‘Open-Source’ Approach to Simple and Precise<br />
Genome Editing with rAAV<br />
Rob Howes, Alex Rieck, Eric Rhodes.<br />
246<br />
UV Light Modulates Transcriptional Activity <strong>of</strong> Egr-1<br />
Promoter on Human Primary Tenocytes<br />
Francisco Martinez-F, Araceli Barrera-Lopez, Hugo Sandoval-<br />
Zamora, David T. Curiel, Juan A. Madinaveitia-V, Rebecca E.<br />
Franco-Bourland.<br />
Fetal and Adult Stem <strong>Cell</strong>s<br />
247<br />
Embryonic Renal Progenitor <strong>Cell</strong>s Activate the<br />
b-Catenin/TCF Signaling Pathway during Integration<br />
into Damaged Adult Renal Tubules<br />
Paul Goodyer, Zhao Zhang, Diana Iglesias.<br />
248<br />
Preclinical Investigations <strong>of</strong> Therapeutic Beneits and<br />
Biodistribution from Stress Erythropoiesis on Minimal<br />
Dose <strong>of</strong> Lysosomal Enzyme Required for Phenotypic<br />
Correction in Mice with Hurler Syndrome<br />
Jingfen Han, Mei Dai, Salim S. Elamouri, Phuong Cao, Dao Pan.<br />
104<br />
<strong>Final</strong> <strong>Program</strong> SALT LAKE CITY, UTAH May 15–18, 2013
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