Final Program - American Society of Gene & Cell Therapy
Final Program - American Society of Gene & Cell Therapy
Final Program - American Society of Gene & Cell Therapy
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Abstract Directory, Friday, May 17, 2013<br />
Poster Session II, continued<br />
5:30 PM - 7:30 PM<br />
Room: Exhibit Hall C/D<br />
Oligonucleotide & RNAi Therapeutics<br />
457<br />
RNA Interference-Based <strong>Gene</strong> <strong>Therapy</strong> for Parkinson’s<br />
Disease Using shRNA That Speciically Targeting the<br />
LRRK2 G2019S Allele<br />
Liang Huang, Xiaomin Su, Juan Wang, Kathleen Maguire-Zeiss,<br />
Howard J. Feder<strong>of</strong>f.<br />
458<br />
An RNAi Screening Platform To Identify Modulators <strong>of</strong><br />
Glioma Stem <strong>Cell</strong>s Viability and Differentiation<br />
Christian E. Badr, Romain Amante, Stephanie Van Hoppe, Bakhos<br />
A. Tannous.<br />
459<br />
Short Hairpin RNAs (shRNA) Against Steroid Receptor<br />
Coactivator-3/Ampliied in Breast Cancer 1 (SRC-3)<br />
and Steroid Receptor Coactivator-1 (SRC-1) as Breast<br />
Cancer Therapeutic Agents<br />
David M. Lonard, Donald Rao, John J. Nemunaitis, Neil N. Senzer,<br />
Bert W. O’Malley.<br />
460<br />
Lentiviral-Mediated ENaCa Knockdown, as a Treatment<br />
for Cystic Fibrosis Lung Disease<br />
Rebekka E. Harding-Smith, Deborah R. Gill, Stephen C. Hyde.<br />
461<br />
Engineering Mammalian <strong>Cell</strong>s To Secrete RNA to the<br />
Extracellular Space<br />
Kevin J. Polach, Leslie Wilkinson, Elaine Brunhoeber, Amy<br />
Pettigrew, Kirby Wallace, Jeff Sparks, Angela Rea-Ramsey, Casey<br />
Pence, Majed Matar, Diane McClure, Jennifer Rice, Khursheed<br />
Anwer, Jason G. Fewell.<br />
462<br />
Lipid-Polymer Mediated siRNA <strong>Therapy</strong> for Silencing<br />
CXCR4 in Acute Myeloid Leukemia<br />
Breanne Landry, Hilal Gül-Uludag, Hasan Uludag.<br />
463<br />
Messenger RNA as a Novel Therapeutic Approach<br />
Antonin de Fougerolles.<br />
464<br />
Development <strong>of</strong> Post-Column Process <strong>of</strong> Immobilized<br />
Colanic Acid Degrading Enzyme Reactor<br />
Chromatography in SuperClean Therapeutic Plasmid<br />
DNA Production<br />
Li Chen, Christopher M. Jay, Nancy S. Templeton, John Nemunaitis,<br />
Nicolas Taquet, Phillip B. Maples.<br />
Pluripotent Stem <strong>Cell</strong>s<br />
465<br />
<strong>Cell</strong> Replacement <strong>Therapy</strong> for Parkinson’s Disease with<br />
Neuronal <strong>Cell</strong>s Derived from Human Parthernogenetic<br />
Stem <strong>Cell</strong><br />
Ibon Garitaonandia, Rodolfo Gonzalez, Alina Ostrowska, Tatiana<br />
Abramihina, Gerald Wambua, Alexander Noskov, Francesca<br />
Boscolo, Louise Laurent, Eugene Redmond, Evan Snyder, Ruslan<br />
Semechkin.<br />
466<br />
<strong>Gene</strong>ration <strong>of</strong> Isogenic Pairs <strong>of</strong> Mutant and<br />
Complemented Fanconi Anemia Human Induced<br />
Pluripotent Stem <strong>Cell</strong>s<br />
Laura I. Marquez, Kathryn Schubert, Feorillo Galivo, Milton<br />
Finegold, Susan Olson, Markus Grompe.<br />
467<br />
Engineering <strong>of</strong> Safety Control Switches for Human<br />
Induced Pluripotent Stem <strong>Cell</strong>s<br />
Wu Ou, Pingjuan Li, Jakob Reiser.<br />
468<br />
Eficient <strong>Gene</strong>ration <strong>of</strong> Integration-Free iPS <strong>Cell</strong>s from<br />
Human Adult Peripheral Blood<br />
Rui-Jun Su, David J. Baylink, Amanda Nieses, Xianmei Meng, Jason<br />
B. Kiroyan, Kimberly J. Payne, Yuyou Duan, Benjamin Tschudy-<br />
Seney, Mary Kearns-Jonker, K.-H William Lau, Xiao-Bing Zhang.<br />
469<br />
iPSC-Based Strategy To Correct the Bleeding Phenotype<br />
in Hemophilia A Targeting FVIII Expression to<br />
Endothelial <strong>Cell</strong>s<br />
Maria Talmon, Gabriella Ranaldo, Chantal Grosso, Angelo<br />
Lombardo, Simone Merlin, Stefania E. Cannizzo, Angel Raya, Luigi<br />
Naldini, Piercarla Schinco, Antonia Follenzi.<br />
470 Abstract Moved to Oral Abstract Session 233<br />
471<br />
Correction <strong>of</strong> DF508 CFTR in Patient-Derived iPS <strong>Cell</strong>s<br />
Using Small Frgement Homologous Replacement<br />
(SFHR) and Transcription Activator-Like Effector<br />
Nucleases (TALENs)<br />
Shingo Suzuki, Thomas J. Cradick, Roy G. Sargent, Lee Albert,<br />
Matthew Porteus, Gang Bao, Dieter C. Gruenert.<br />
472<br />
Directed Differentiation <strong>of</strong> Human Induced Pluripotent<br />
Stem (hiPS) <strong>Cell</strong>s into Functional Parathyroid Tissue<br />
for <strong>Cell</strong> <strong>Therapy</strong><br />
Alaleh Esmaeili Shandiz, Albert Lee, Shingo Suzuki, R. G. Sargent,<br />
Michael H. Yezzi, Lisa A. Orl<strong>of</strong>f, Dieter C. Gruenert.<br />
473<br />
iPSC-Derived Cardiomyocytes from the Urine <strong>of</strong> a<br />
Patient with Duchenne Muscular Dystrophy<br />
Xuan Guan, David Mack, Yingai Shi, Chad Markert, Guihua Liu,<br />
Michael Lawlor, Emily Mooreield, Tara Jones, Mark Furth,<br />
Yuanyuan Zhang, Martin K. Childers.<br />
Friday, May 17, 2013<br />
<strong>Final</strong> <strong>Program</strong> SALT LAKE CITY, UTAH May 15–18, 2013<br />
121
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