Final Program - American Society of Gene & Cell Therapy
Final Program - American Society of Gene & Cell Therapy
Final Program - American Society of Gene & Cell Therapy
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Abstract Directory, Friday, May 17, 2013<br />
Friday, May 17, 2013<br />
Poster Session II, continued<br />
5:30 PM - 7:30 PM<br />
Room: Exhibit Hall C/D<br />
Pluripotent Stem <strong>Cell</strong>s<br />
474<br />
Process Development for Scalable Manufacturing <strong>of</strong><br />
hESC-Derived Cardiomyocytes<br />
Vincent C. Chen, Jingjing Ye, Giau Hua, Ziguang Lin, Dalin Chen,<br />
Aparna Roy, Patricia Huang, Wei Dang, Josh Tompkins, Arthur<br />
Riggs, Wenyi Chen, Joseph Wu, David Hsu, Larry Couture.<br />
475 Abstract Withdrawn from Presentation<br />
476<br />
Development and Qualiication <strong>of</strong> Assays To<br />
Characterize Human Embryonic Stem <strong>Cell</strong>s (hESC) and<br />
hESC-Derived Products at the Center <strong>of</strong> Biomedicine<br />
and <strong>Gene</strong>tics (CBG)<br />
Patricia Huang, Aparna Krishnan, Wei Dang, Vincent Chen, Jing<br />
Jing Ye, Aparna Roy, Patricia Lopez, Jing Chai, Ruilin Wu, Tania<br />
Aguilar, David Hsu, Larry Couture.<br />
Late Breaking Abstracts II<br />
701 Abstract Withdrawn from Presentation<br />
702<br />
Preclinical study <strong>of</strong> a scAAV2/8-Lp1-huPPCA vector in<br />
the treatment <strong>of</strong> the galactosialidosis mouse model<br />
Huimin Hu, Elida Gomero, Erik Bonten, John T Gray, Arthur<br />
Nienhuis, Alessandra d’Azzo<br />
703<br />
Improved Retroviral Replicating Vectors for Prodrug-<br />
Activator <strong>Gene</strong> <strong>Therapy</strong> <strong>of</strong> Cancer<br />
Noriyuki Kasahara, Christopher Logg, Omar Perez, Oscar Diago,<br />
Ryan Burnett, Aki Inagaki, Amy Lin, Cindy Burrascano, Mitchel<br />
Berger, Kryst<strong>of</strong> Bankiewicz, Weijun Wang, Hyun Kim, Walter Wolf,<br />
Thomas Chen, Kenneth Cornetta, Carlos Ibañez, Joan Robbins,<br />
Harry Gruber, Douglas J. Jolly<br />
704<br />
The recombinant tight junction opener JO-1* decreases<br />
hypoxia in tumors<br />
Kamola Saydaminova, Roma Yumul, Christine Wang, Akseli<br />
Hemminki, Andre Lieber<br />
705<br />
Development <strong>of</strong> a Clinical AAV-Based Vector Encoding<br />
a Microdystrophin Transgene for the Treatment <strong>of</strong><br />
Duchenne Muscular Dystrophy<br />
Yoshiaki Miura, Joohee Han, Julia Davydova, Masato Yamamoto<br />
706<br />
Novel therapeutic nanoparticles for in vivo delivery <strong>of</strong><br />
low dose siRNA in liver cells and for the treatment <strong>of</strong><br />
liver ibrosis associated nonalcoholic steatohepatitis<br />
Xavier de Mollerat du Jeu, Akiko Eguchi, Andronikou Nektaria,<br />
Ariel E. Feldsteinand, Peter Welch<br />
707<br />
Directed evolution <strong>of</strong> artiicial viruses<br />
Ir. Erik Teunissen, Dr. Enrico Mastrobattista Pr<strong>of</strong>. Dr. Peter Rottier,<br />
Pr<strong>of</strong>. Dr. Daan Crommelin<br />
708<br />
The NanoAssemblr Platform: Microluidics-based<br />
Manufacture <strong>of</strong> Limit Size Lipid Nanoparticles for<br />
Nucleic Acid Delivery<br />
J. Taylor, C. Walsh, N. Belliveau, P. Lin, R. Rungta, H. Choi, J. Lee, E.<br />
Ramsay, T. Leaver, A. Wild, K. Ou, A. Leung, Y. Tam, I. Hafez, S. Chen,<br />
B. MacVicar, C. Hansen, P. Cullis<br />
709<br />
Preclinical development <strong>of</strong> an AAV vector for the<br />
treatment <strong>of</strong> X-linked retinitis pigmentosa due to<br />
RPGRorf15 mutation<br />
Zhijian Wu, Suja Hiriyanna, Haohua Qian, Suddhasil Mookherjee,<br />
Kayleigh Kaneshiro, Maria Campos, Chun Gao, Robert Fariss,<br />
Anand Swaroop, Tiansen Li, Peter Colosi<br />
710<br />
Cytotoxic T-cell Surface Engineering with Chemically<br />
Self-Assembled Antibody Nanorings (CSANS)<br />
C. R. Wagner, Kari Gabrielse, Dr. Jae Chul Lee<br />
711<br />
Speciic siRNA delivery to primary activated T cells for<br />
anti-inlammatory therapy<br />
Na Hyung Kim, Yuran Xie, Archana Thakur, Lawrence Lum, Olivia<br />
Merkel<br />
712<br />
MicroRNA-155 confers encephalogenic potential to<br />
Th17 cells by promoting effector gene expression<br />
Ruozhen Hu, Thomas B. Huffaker, Dominique A. Kagele, Marah C.<br />
Runtsch, Erin Bake, Aadel A. Chaudhuri, June L. Round, Ryan M.<br />
O’Connell<br />
713<br />
DNA Mini Strings: The Gold Standard for Transgene<br />
Delivery<br />
Naiseh Naissi, Roderick Slavcev<br />
714<br />
Restoring a minimal motor unit potential and<br />
peripheral motor conductivity in lower extremities in<br />
a 15 years old girl with complete loss <strong>of</strong> spinal cord<br />
continuity at Th2-Th3 after combine autologous bone<br />
marrow derived cells and mesenchymal stem cells tr<br />
Jarocha Danuta, Milczarek Olga, Kwiatkowski Stanislaw, Majka<br />
Marcin<br />
715<br />
Genomic correction <strong>of</strong> Duchenne Muscular Dystrophy<br />
patient-derived iPSCs using TALENs<br />
Hongmei Li, Naoko Fujimoto, Noriko Sasakawa, Takashi<br />
Yamamoto, Knut Woltjen, Hidetoshi Sakurai, Shinya Yamanaka,<br />
Akitsu Hotta<br />
122<br />
<strong>Final</strong> <strong>Program</strong> SALT LAKE CITY, UTAH May 15–18, 2013
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