Final Program - American Society of Gene & Cell Therapy
Final Program - American Society of Gene & Cell Therapy
Final Program - American Society of Gene & Cell Therapy
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Abstract Directory, Friday, May 17, 2013<br />
Poster Session II, continued<br />
5:30 PM - 7:30 PM<br />
Room: Exhibit Hall C/D<br />
Hematologic and Immunologic <strong>Gene</strong> & <strong>Cell</strong><br />
<strong>Therapy</strong> I<br />
425<br />
Evaluating a LM-PCR and Pyrosequencing Method<br />
for the Detection <strong>of</strong> Clonal Contribution in Polyclonal<br />
Retrovirally Transduced Samples<br />
Martijn H. Brugman, Julia D. Suerth, Michael Rothe, Sebastian<br />
Suerbaum, Axel Schambach, Ute Modlich, Olga S. Kustikova,<br />
Christopher Baum.<br />
426<br />
Disease Modeling Using Induced Pluripotent Stem <strong>Cell</strong>s<br />
Derived from Severe Congenital Neutropenia Patients<br />
Lisa Trump, Ramesh Nayak, Jose Cancelas, Carolyn Lutzko.<br />
427<br />
Enhanced Engraftment <strong>of</strong> Murine and Human<br />
Hematopoietic Stem <strong>Cell</strong>s Mobilized Using the<br />
Plerixafor+G-CSF Combination<br />
Nikoleta Psatha, Garyfalia Karponi, Eleni Sgouramali, Athanasios<br />
Siametis, Panayotis Baliakas, Isabelle Riviere, Michel Sadelain,<br />
Achilles Anagnostopoulos, George Stamatoyannopoulos, Thalia<br />
Papayannopoulou, Evangelia Yannaki.<br />
428<br />
Evaluation <strong>of</strong> Engraftment and Tolerance Induction<br />
after Reduced Intensity Conditioning for Hematopoietic<br />
Stem <strong>Cell</strong> Transplantation in the Rhesus <strong>Gene</strong> <strong>Therapy</strong><br />
Model<br />
Naoya Uchida, Molly Evans, Richard Weitzel, Aylin Bonifacino,<br />
Sandra Price, Allen Krouse, Mark Metzger, Matthew Hsieh, Robert<br />
Donahue, John Tisdale.<br />
429<br />
Myeloprotective Properties <strong>of</strong> Inducible (shRNA-<br />
Mediated) Knock-Down <strong>of</strong> Deoxycytidine-Kinase (dCK)<br />
in Human Hematopoietic In Vitro Models<br />
Nico Lachmann, Kevin Czarnecki, Miriam Hetzel, Sebastian<br />
Brennig, Niels Heinz, Bernd Schiedlmeier, Thomas Moritz.<br />
430<br />
Comparision <strong>of</strong> In-Utero <strong>Gene</strong> <strong>Therapy</strong> and In-Utero<br />
Hemopoietic Stem <strong>Cell</strong> <strong>Therapy</strong> Approaches in Severe<br />
Models <strong>of</strong> Murine beta Thalassemia<br />
Niraja Dighe, Citra Mattar, Lay Geok Tan, Daren Sandikin, Simon<br />
Waddington, Michael Antoniou, Mahesh Choolani, Jerry Chan.<br />
431<br />
Regulatory T <strong>Cell</strong>s Suitable for Clinical Use Can Be<br />
Propagated on Artiicial Antigen Presenting <strong>Cell</strong>s<br />
Pappanaicken Kumaresan, Chetan Dhamne, Sourindra Maiti,<br />
Janani Krishnamoorthy, Radhika Thokala, Helen Huls, Champlin<br />
Richard, Dean Lee, Dat Tran, Laurence Cooper.<br />
<strong>Gene</strong> and <strong>Cell</strong> <strong>Therapy</strong> for Pulmonary<br />
Diseases<br />
432 Abstract Moved to Oral Abstract Session 237<br />
433<br />
Eficient <strong>Gene</strong> Delivery to Pig Airway Epithelia<br />
and Submucosal Glands Using Helper-Dependent<br />
Adenoviral Vectors<br />
Huibi Cao, Tiago N. Machuca, Jonathan Yeung, Jing Wu, Kai Du,<br />
Cathleen Duan, Riccardo Bonato, Allan L. Coates, Kitty Leung,<br />
Herman Yeger, Ernest Cutz, Mingyao Liu, Shaf Keshavjee, Jim Hu.<br />
434<br />
Minicircle Plasmids Result in Enhanced and Prolonged<br />
Transgene Expression <strong>of</strong> Airway Epithelial <strong>Cell</strong>s Both In<br />
Vitro and In Vivo<br />
Mustafa M. Munye, Rachel E. Brown, Aristides D. Tagalakis,<br />
Josephine L. Barnes, Rupinder K. Ghatrora, Martin Pule, Mark F.<br />
Lythgoe, Robin J. McAnulty, Steven J. Howe, Stephen L. Hart.<br />
435<br />
Novel Human Bronchial Epithelial <strong>Cell</strong> Lines for the<br />
Study <strong>of</strong> <strong>Gene</strong> <strong>Therapy</strong> Approaches To Treat Primary<br />
Ciliary Dyskinesia<br />
Mustafa M. Munye, Claire M. Smith, Rob A. Hirst, Amelia Shoemark,<br />
Juliette M. Delhove, Tristan R. Mckay, Claire Hogg, Christopher<br />
O’Callaghan, Steven J. Howe, Stephen L. Hart.<br />
436<br />
Upregulation <strong>of</strong> a Cluster <strong>of</strong> microRNAs on Mouse<br />
Chromosome 12qF1 in a Kras Mutant Mouse Model <strong>of</strong><br />
Lung Adenocarcinoma<br />
Paul N. Valdmanis, Biswajoy Roy-Chaudhuri, Hak Kyun Kim,<br />
Leanne C. Sayles, Yanyan Zheng, Chen-Hua Chuang, Debbie<br />
Caswell, Monte Winslow, E. A. Sweet-Cordero, Mark A. Kay.<br />
437<br />
Lentiviral-Mediated Functional Correction <strong>of</strong><br />
Hermansky-Pudlak Syndrome Type 1 Melanocytes<br />
Yasuhiro Ikawa, Richard Hess, Heidi Dorward, Bernadette<br />
Gochuico, William A. Gahl, Fabio Candotti.<br />
438<br />
Development <strong>of</strong> a Myeloid <strong>Cell</strong>-Binding Adenovirus for<br />
the Potential <strong>Gene</strong> <strong>Therapy</strong> <strong>of</strong> Alpha-1 Anti-Trypsin<br />
Deiciency<br />
Maurizio Buggio, Christopher Towe, Michael O. Alberti, Justin C.<br />
Roth, Anand C. Annan, David T. Curiel.<br />
439<br />
MicroRNAs as Potential Targets for <strong>Therapy</strong> <strong>of</strong><br />
Pulmonary Hypertension<br />
Igor B. Gubrij, Amanda K. Pangle, Li Pang, Larry G. Johnson.<br />
440<br />
CVB3 Infection Elicits Potent Oncolytic Activity Against<br />
Lung Cancer Stem <strong>Cell</strong>s<br />
Miyako Sagara, Hiroyuki Inoue, Shohei Miyamoto, Chika Sakamoto,<br />
Yuki Nakano, Koichi Takayama, Hiroyuki Shimizu, Yoichi<br />
Nakanishi, Kenzaburo Tani.<br />
Friday, May 17, 2013<br />
<strong>Final</strong> <strong>Program</strong> SALT LAKE CITY, UTAH May 15–18, 2013<br />
119
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