Final Program - American Society of Gene & Cell Therapy
Final Program - American Society of Gene & Cell Therapy
Final Program - American Society of Gene & Cell Therapy
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Abstract Directory, Saturday, May 18, 2013<br />
Poster Session III, continued<br />
3:45 PM - 5:45 PM<br />
Room: Exhibit Hall C/D<br />
Hematologic and Immunologic <strong>Gene</strong> & <strong>Cell</strong><br />
<strong>Therapy</strong> II<br />
Late Breaking Abstracts III<br />
733<br />
Correction <strong>of</strong> canine Factor VII (FVII) deiciency by<br />
AAV-mediated expression <strong>of</strong> canine FVII zymogen<br />
Paris Margaritis, Dwight A. Bellinger, Shangzhen Zhou, Armida<br />
Faella, Timothy C. Nichols, Katherine A. High<br />
668<br />
Engineering <strong>of</strong> a HIV-Resistant Immune System with<br />
Hematopoietic Stem <strong>Cell</strong>s – A Polycistronic Approach<br />
Janet Chung, Chy-Anh Tran, Angel Gu, Lisa Scherer, Haitang Li,<br />
David L. DiGiusto, John J. Rossi.<br />
669<br />
Direct and Indirect Immune Suppressive Effects <strong>of</strong> High<br />
Hepatic Expression Direct Effective Reversal <strong>of</strong> Factor<br />
IX Inhibitors by AAV <strong>Gene</strong> Transfer<br />
David Markusic, Roland Herzog.<br />
670<br />
Combination <strong>Therapy</strong> <strong>of</strong> Anti-CD20, AMD3100, G-CSF<br />
and Factor VIII Plasmid-Mediated <strong>Gene</strong> <strong>Therapy</strong><br />
Can Successfully Promote Tolerance to Factor VIII in<br />
Hemophilia A Mice with Pre-Existing Inhibitors<br />
Chao Lien Liu, Meghan Lyle, Simon C. Shin, Carol H. Miao.<br />
671<br />
Identiication <strong>of</strong> Novel Chromatin Insulator<br />
Elements for Use in Lentiviral <strong>Gene</strong> <strong>Therapy</strong> <strong>of</strong> T <strong>Cell</strong><br />
Immunodeiciencies<br />
Sheng Zhou, Taihe Lu, Zhijun Ma, John T. Gray, Brian P. Sorrentino.<br />
672<br />
Transduction <strong>of</strong> Human CD34+ <strong>Cell</strong>s in the NOD SCIDg<br />
(NSG) Mouse Model Using Lenti-hWASP-Vectors Derived<br />
from Stable Producer Clones<br />
Matthew M. Wielgosz, Yoon S. Kim, Robert E. Throm, Gael G.<br />
Carney, John T. Gray, Arthur W. Nienhuis.<br />
673<br />
Pre-Clinical Modeling <strong>of</strong> Foamy Virus Vector Based<br />
<strong>Gene</strong> <strong>Therapy</strong> for SCID-X1<br />
Gabrielle M. Curinga, Iram Khan, Swati Singh, Joey Pangallo, Brian<br />
Beard, Troy Torgerson, Andrew Scharenberg, Grant Trobridge,<br />
Hans-Peter Kiem, David Rawlings.<br />
674<br />
Long Term Safety <strong>of</strong> Clinical Grade LentiGlobin Vectors<br />
in a b-Thalassemic and Normal Mice<br />
Olivier Negre, Cynthia Bartholoma, Robert Kutner, Beatrix Gillet-<br />
Legrand, Celine Courne, Anais Paulard, Byoung Ryu, Maria Denaro,<br />
Christ<strong>of</strong> von Kalle, Emmanual Payan, Michell Finer, Gabor Veres.<br />
675 Abstract Withdrawn from Presentation<br />
734 Abstract Withdrawn from Presentation<br />
735<br />
Optimization <strong>of</strong> dual-function vectors for Alpha-1<br />
Antitrypsin Deiciency<br />
Qiushi Tang, Christian Mueller, Lina Song, Terence Flotte<br />
736<br />
Targeting dendritic cells with lentiviral vectors induces<br />
tolerance <strong>of</strong> effector T cells and protects mice from<br />
experimental autoimmune encephalomyelitis<br />
Bruna de Andrade Pereira, Mathias Ackermann, Christiane Dresch,<br />
Cornel Fraefel<br />
737<br />
Novel adenoviral vectors induce robust T cell responses<br />
to HSV2 and signiicantly boost responses after repeat<br />
homologous administration<br />
Christopher A. Lazarski, Douglas E. Brough, Lisa L. Wei<br />
738<br />
TALEN-based Individualized <strong>Gene</strong> Medicine for<br />
Epidermolysis Bullosa<br />
Mark J. Osborn, Colby G. Starker, Amber N. McElroy, Beau R.<br />
Webber, Anthony P. DeFeo, Richard Gabriel, Manfred Schmidt,<br />
Christ<strong>of</strong> von Kalle, Daniel F. Carlson, Morgan L. Maeder, J. Keith<br />
Joung, John E. Wagner, Daniel F. Voytas, Bruce R. Blazar, Jakub<br />
Tolar<br />
739<br />
Prevention <strong>of</strong> Anti-Capsid Immune Response Following<br />
Systemic AAV9 Dosing in Infant Rhesus Monkeys<br />
Darin Falk<br />
740<br />
Inhibition <strong>of</strong> ocular neovascularization by<br />
subconjunctival gene delivery <strong>of</strong> calreticulin-derived<br />
peptide, vasostatin 112<br />
Guei-Sheung Liu, Youn-Shen Bee, Gregory J. Dusting, Ming-Hong<br />
Tai<br />
741<br />
Transient Epigenetic <strong>Gene</strong> <strong>Therapy</strong> as a New<br />
Therapeutic/Prophylactic Avenue for Aging/<br />
Degenerative Diseases and Neurodevelopmental<br />
Disorders<br />
Roger Bertolotti<br />
742<br />
Successful Systemic Cancer Targeting by Adenovirus<br />
Vector with AB-loop Redesigned Fiber via Reducing<br />
Liver Sequestration<br />
Yoshiaki Miura, Joohee Han, Julia Davydova, Masato Yamamoto<br />
Saturday, May 18, 2013<br />
<strong>Final</strong> <strong>Program</strong> SALT LAKE CITY, UTAH May 15–18, 2013<br />
137
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