Final Program - American Society of Gene & Cell Therapy
Final Program - American Society of Gene & Cell Therapy
Final Program - American Society of Gene & Cell Therapy
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Friday, May 17, 2013<br />
Abstract Directory, Friday, May 17, 2013<br />
Oral Abstract Session 323, continued<br />
Musculo-skeletal <strong>Gene</strong> & <strong>Cell</strong> <strong>Therapy</strong> II<br />
1:00 PM - 3:00 PM<br />
Room: 150 DEFG<br />
294 2:00 PM<br />
Restriction <strong>of</strong> Calpain3 Expression to the Skeletal<br />
Muscle Prevents Cardiac Toxicity and Corrects<br />
Pathology in a Murine Model <strong>of</strong> Limb-Girdle Muscular<br />
Dystrophy<br />
Carinne Roudaut, Florence Le Roy, Laurence Suel, Isabelle Richard.<br />
295 2:15 PM<br />
RNAi <strong>Therapy</strong> for Limb Girdle Muscular Dystrophy<br />
Type 1A<br />
Jian Liu, Lindsay Wallace, Sara Garwick-Coppens, Carol Davis,<br />
Chady Hakim, Susan Guckes, Michael Hauser, Jerry Mendell, Susan<br />
Brooks, Scott Harper.<br />
296 2:30 PM<br />
Expression <strong>of</strong> FKRP Consequently Restored Functional<br />
Glycosylation <strong>of</strong> a-DG in the Skeletal and Cardiac<br />
Muscles in FKRP Mutant Mice<br />
Qi Long Lu, Lei Xu, Pei Juan Lu, Chi-Hsien Wang, Elizabeth<br />
Keramaris, Chunping Qiao, Bin Xiao, Derek J. Blake, Xiao Xiao.<br />
297 2:45 PM<br />
Minimally Invasive Implantation <strong>of</strong> Autologous<br />
Chondrocytes Transduced with rAAV5-IGF-I Improves<br />
Longterm Cartilage Repair in Full-Thickness Chondral<br />
Defects in the Equine Model<br />
Kyla Ortved, Alan J. Nixon.<br />
Oral Abstract Session 324<br />
Cancer-Targeted <strong>Gene</strong> & <strong>Cell</strong> <strong>Therapy</strong><br />
1:00 PM - 3:00 PM<br />
Room: Ballroom C<br />
298 1:00 PM<br />
Safety and Correlates <strong>of</strong> Clinical Response in an Early<br />
Phase Clinical Trial in Multiple Myeloma Patients<br />
Post Auto-SCT and Adoptive Immunotherapy with<br />
Engineered T <strong>Cell</strong>s Expressing an HLA-A2 Restricted<br />
Afinity-Enhanced TCR for LAGE-1 and NY-ESO-1<br />
Bruce L. Levine, Aaron P. Rapoport, Edward A. Stadtmauer, Dan<br />
T. Vogl, Brendan Weiss, Gwendolyn K. Binder-Scholl, Dominic P.<br />
Smethurst, Jeffrey Finkelstein, Irina Kulikovskaya, Minnal Gupta,<br />
Erica Suppa, Joanna E. Brewer, Alan D. Bennett, Andrew B. Gerry,<br />
Nick J. Pumphrey, Helen K. Tayton-Martin, Daniel Williams,<br />
Zhaohui Zheng, Ashraf Z. Badros, Saul Yanovich, Gorgon Akpek,<br />
Michael Kalos, Bent K. Jakobsen, Carl H. June.<br />
299 Abstract Moved to Oral Abstract Session 230<br />
648 1:15 PM<br />
Neural Stem <strong>Cell</strong>s Expressing a Modiied Human<br />
Carboxylesterase Potentiate Anti-Cancer Activity <strong>of</strong><br />
Irinotecan in Murine Glioma Model<br />
Karen S. Aboody, Lucy Y. Ghoda, Margarita Gutova, Megan<br />
Gilchrist, Christine Brown, Vazgen Kankaldyyan, Elizabth Garcia,<br />
Lauren H<strong>of</strong>fman, Rex A. Moats, Phil Potter, Timothy W. Synold,<br />
Michael Barish.<br />
300 1:30 PM<br />
Virus-Speciic Cytotoxic T Lymphocytes (CTLs)<br />
Redirected with a Chimeric Antigen Receptor (CAR)<br />
and Engineered To Respond to IL7 Resist Regulatory T<br />
<strong>Cell</strong> (Treg) Inhibition<br />
Serena K. Perna, Daria Pagliara, Aruna Mahendravada, Hao Liu,<br />
Malcolm K. Brenner, Barbara Savoldo, Gianpietro Dotti.<br />
301 1:45 PM<br />
Engineering Hematopoiesis for Tumor-Targeted<br />
Delivery <strong>of</strong> IFNa by Tumor-Iniltrating Macrophages<br />
Achieves Safe and Effective Inhibition <strong>of</strong> Breast<br />
Cancer and Its Metastases in Both Murine and Human<br />
Hematochimeric Models<br />
Giulia Escobar, Davide Moi, Anna Ranghetti, Mario L. Squadrito,<br />
Michele De Palma, Roberta Mazzieri, Luigi Naldini.<br />
302 2:00 PM<br />
Myeloid Suppressor <strong>Cell</strong> Blockade Potentiates Anti-<br />
Tumor Responses <strong>of</strong> Adoptive T <strong>Cell</strong> Transfer <strong>Therapy</strong><br />
Steven Mok, Christopher Tsui, Thinle Chodon, Antoni Ribas,<br />
Richard C. Koya.<br />
303 2:15 PM<br />
Afinity-Enhanced Epithelial Junction Openers Improve<br />
Cancer Chemotherapy<br />
Roma Yumul, Hua Cao, Maximillian Richter, Julie Gralow, Andre<br />
Lieber.<br />
304 2:30 PM<br />
Glioblastoma Transfer miRNAs into Microglial <strong>Cell</strong>s<br />
through Extracellular Vesicles<br />
Erik R. Abels, Kristan E. van der Vos, Johan Skog, Suzanne E.<br />
Hickman, Joseph El Khoury, Xandra O. Breakeield.<br />
305 2:45 PM<br />
ab-T <strong>Cell</strong> Receptor-Based <strong>Gene</strong> <strong>Therapy</strong> Targeting<br />
the Common Tumor-Antigen Survivin for <strong>Therapy</strong> <strong>of</strong><br />
Hematological Malignancies<br />
Caroline Arber, Harshal Abhyankar, Helen E. Heslop, Gianpietro<br />
Dotti, Barbara Savoldo.<br />
110<br />
<strong>Final</strong> <strong>Program</strong> SALT LAKE CITY, UTAH May 15–18, 2013
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