Final Program - American Society of Gene & Cell Therapy
Final Program - American Society of Gene & Cell Therapy
Final Program - American Society of Gene & Cell Therapy
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Abstract Directory, Friday, May 17, 2013<br />
Oral Abstract Session 321, continued<br />
<strong>Gene</strong> & <strong>Cell</strong> <strong>Therapy</strong> <strong>of</strong> Diabetes, Metabolic<br />
and <strong>Gene</strong>tic Diseases I<br />
1:00 PM - 3:00 PM<br />
Room: Ballroom B<br />
281 2:45 PM<br />
AAV-Based over Expression <strong>of</strong> PEPCK-C Re-Patterns<br />
Mouse Muscle Energy Metabolism and Prevents High-<br />
Fat Diet Induced Obesity<br />
Daibang Nie, Sheri Wang, Ying Tang, Dong Wei, William Witt, Allan<br />
Zhao, Yifan Dai, Freddie Fu, Johnny Huard, Bing Wang.<br />
Oral Abstract Session 322<br />
Neurological <strong>Therapy</strong>: Neurodegeneration<br />
and Imaging<br />
1:00 PM - 3:00 PM<br />
Room: 150 ABC<br />
287 2:15 PM<br />
Fusion <strong>of</strong> Either Gap-43 or Tau to the Clostridial<br />
Tetanus Toxin Light Chain Improves Synaptic Inhibition<br />
in the Rat Spinal Cord Following Adenoviral Vector<br />
<strong>Gene</strong> Delivery<br />
Eleanor M. Donnelly, Chalonda R. Handy, Marie Kim, Jeremiah<br />
Huang, Thais Federici, Nicholas M. Boulis.<br />
288 2:30 PM<br />
MR-Guided Delivery <strong>of</strong> AAV2-hAADC into the Midbrain<br />
<strong>of</strong> Macaques Results in a Safe and Eficient Axonal<br />
Transport <strong>of</strong> AADC into the Striatum<br />
Kryst<strong>of</strong> S. Bankiewicz, Adrian P. Kells, Lluis Samaranch, Waldy San<br />
Sebastian, Nitasha Sharma, John Bringas, Phillip Pivirotto, John<br />
Forsayeth.<br />
289 2:45 PM<br />
Noninvasive, Quantitative PET Imaging <strong>of</strong> AAV-<br />
Mediated D2R80A Reporter <strong>Gene</strong> Expression in Live<br />
Animal Brains<br />
Sea Young Yoon, Datta Ponde, Harish Poptani, Jessica Bagel,<br />
Patricia A. O’Donnell, Charles H. Vite, John H. Wolfe.<br />
282 1:00 PM<br />
Silencing Mutant Htt by AAV-Mediated Expression <strong>of</strong><br />
RNAi Ameliorates Disease Manifestations in the YAC128<br />
Mouse Model <strong>of</strong> Huntington’s Disease<br />
Lisa M. Stanek, Lamya S. Shihabuddin, Seng H. Cheng.<br />
283 1:15 PM<br />
<strong>Gene</strong> Transfer <strong>of</strong> Human Apoe e2 Alleviate the<br />
Progression <strong>of</strong> Amyloid Deposition In Vivo<br />
Eloise Hudry, Jonathan Dashk<strong>of</strong>f, Allyson Lee, Shuko Takeda,<br />
Robert M. K<strong>of</strong>ie, Tadafumi Hashimoto, Maria Scheel, Tara Spires-<br />
Jones, Michal Arbel-Ornath, Rebecca A. Betensky, Beverly L.<br />
Davidson, Bradley T. Hyman.<br />
284 1:30 PM<br />
Vascular Delivery <strong>of</strong> AAV9-RNAi as a Potential <strong>Therapy</strong><br />
for Huntington’s Disease<br />
Brett Dufour, Catherine Smith, Randall Clark, Timothy Walker, Jodi<br />
McBride.<br />
285 1:45 PM<br />
Transcriptional Targeting <strong>of</strong> HSV Vector-Mediated<br />
Transgene Expression to Speciic Sensory Neuron<br />
Subtypes<br />
Mark F. Doyal, Mingdi Zhang, George Huang, Justus Cohen, Nicole<br />
Scheff, Michael Gold, William F. Goins, Joseph C. Glorioso.<br />
Oral Abstract Session 323<br />
Musculo-skeletal <strong>Gene</strong> & <strong>Cell</strong> <strong>Therapy</strong> II<br />
1:00 PM - 3:00 PM<br />
Room: 150 DEFG<br />
290 1:00 PM<br />
<strong>Gene</strong> <strong>Therapy</strong> Combined with NF-kappaB Inhibition for<br />
Duchenne Muscular Dystrophy<br />
Ying Tang, Robert Kang, Kara Imbrogno, Arvydas Usas, Qing Yang,<br />
Aiping Lu, Freddie Fu, Johnny Huard, Bing Wang.<br />
291 1:15 PM<br />
AAV Mediated Overexpression <strong>of</strong> Human a7 Integrin<br />
Leads to Histological and Functional Improvement in<br />
Dystrophic Mice<br />
Kristin N. Heller, Chrystal L. Montgomery, Kimberly M. Shontz,<br />
Paul M. L. Janssen, K. Reed Clark, Jerry R. Mendell, Louise R.<br />
Rodino-Klapac.<br />
292 1:30 PM<br />
<strong>Gene</strong>tic Correction <strong>of</strong> Duchenne Muscular Dystrophy<br />
Using Zinc Finger Nucleases<br />
David G. Ousterout, Pablo Perez-Pinera, Pratiksha I. Thakore,<br />
Matthew T. Brown, Charles A. Gersbach.<br />
Friday, May 17, 2013<br />
286 2:00 PM<br />
Mechanisms <strong>of</strong> Caspase-1 Mediated Schwannoma<br />
Regression<br />
Mehran Taherian, Shilpa Prabhakar, Giulia Fulci, Miguel Sena-<br />
Esteves, Xandra O. Breakeield, Gary J. Brenner.<br />
293 1:45 PM<br />
New TALENs To Correct the Reading Frame <strong>of</strong> Exon 54<br />
<strong>of</strong> the Dystrophin <strong>Gene</strong><br />
Joel Rousseau, Jean-Paul Iyombe, Charles A. Gersbach, Jacques P.<br />
Tremblay.<br />
<strong>Final</strong> <strong>Program</strong> SALT LAKE CITY, UTAH May 15–18, 2013<br />
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