Clinical Biochemistry of Domestic Animals (Sixth Edition) - UMK ...

44
Chapter | 2 Comparative Medical Genetics
transfer vector to neural progenitors in the murine brain . Mol. Ther.
11 , 382 – 389 .
Stein , C. S. , Pemberton , J. L. , van Rooijen , N. , and Davidson , B. L.
(1998 ). Effects of macrophage depletion and anti-CD40 ligand on
transgene expression and redosing with recombinant adenovirus .
Gene Ther. 5 , 431 – 439 .
Stewart , E. A. , McKusick , K. B. , Aggarwal , A. , Bajorek , E. , Brady , S. ,
Chu , A. , Fang , N. , Hadley , D. , Harris , M. , Hussain , S. , Lee , R. ,
Maratukulam , A. , O’Connor , K. , Perkins , S. , Piercy , M. , Qin , F. , Reif ,
T. , Sanders , C. , She , X. , Sun , W. L. , Tabar , P. , Voyticky , S. , Cowles , S. ,
Fan , J. B. , Mader, C., Quackenbush, J., Myers, R. M., and Cox , D. R.
( 1997 ). An STS-based radiation hybrid map of the human genome .
Genome Res. 7 ( 5 ) , 422 – 433 .
Tarui , S. , Okuno , G. , Ikura , Y. , Tanaka , T. , Suda , M. , and Nishikawa , M.
( 1965 ). Phosphofructokinase deficiency in skeletal muscle. A new
type of glycogenosis . Biochem. Biophys. Res. Commun. 19 , 517 – 523 .
Taylor , R. M. , Farrow , B. R. , Stewart , G. J. , and Healy , P. J. ( 1986 ).
Enzyme replacement in nervous tissue after allogeneic bone-marrow
transplantation for fucosidosis in dogs . Lancet 2 , 772 – 774 .
Van de Sluis , B. , Wijmenga , C. , and van Oost , B. (2006 ). Copper toxicosis
in Bedlington terriers . In “ The Dog and Its Genome ” ( E. A. Ostrander ,
U. Giger , and K. Lindblad-Toh , Eds.), pp. 348–377 . Cold Spring
Harbor Laboratory Press , New York .
Verma , I. M. , and Weitzman , M. D. ( 2005 ). Gene therapy: twenty-first
century medicine . Annu. Rev. Biochem. 74 , 711 – 738 .
Vite , C. H. , McGowan , J. C. , Niogi , S. N. , Passini , M. A. , Drobatz , K. J. ,
Haskins , M. E. , and Wolfe , J. H. ( 2005 ). Effective gene therapy for
an inherited CNS disease in a large animal model . Ann. Neurol. 57 ,
355 – 364 .
Vogler , C. , Levy , B. , Grubb , J. H. , Galvin , N. , Tan , Y. , Kakkis , E. ,
Pavloff , N. , and Sly , W. S. ( 2005 ). Overcoming the blood-brain barrier
with high-dose enzyme replacement therapy in murine mucopolysaccharidosis
VII . Proc. Natl. Acad. Sci. USA 102 ( 41 ) , 14777 – 14782 .
Vogler , C. , Sands , M. S. , Galvin , N. , Levy , B. , Thorpe , C. , Barker , J. ,
and Sly , W. S. ( 1998 ). Murine mucopolysaccharidosis type VII: the
impact of therapies on the clinical course and pathology in a murine
model of lysosomal storage disease . J. Inherit. Metab. Dis. 21 ( 5 ) ,
575 – 586 .
Walkley , S. U. , Thrall , M. A. , Dobrenis , K. , Huang , M. , March , P. A. ,
Siegel , D. A. , and Wurzelmann , S. ( 1994 ). Bone marrow transplantation
corrects the enzyme defect in neurons of the central nervous
system in a lysosomal storage disease . Proc. Natl. Acad. Sci. USA 91 ,
2970 – 2974 .
Whitney , K. M. , Goodman , S. A. , Bailey , E. M. , and Lothrop , C. D.
( 1994 ). The molecular basis of canine pyruvate kinase deficiency .
Exp. Hematol. 22 , 866 – 874 .
Wolfe , J. H. , Sands , M. S. , Barker , J. E. , Gwynn , B. , Rowe , L. B. ,
Vogler , C. A. , and Birkenmeier , E. H. ( 1992 ). Reversal of pathology
in murine mucopolysaccharidosis type VII by somatic cell gene
transfer . Nature 360 , 749 – 753 .
Wong , L. F. , Azzouz , M. , Walmsley , L. E. , Askham , Z. , Wilkes , F. J. ,
Mitrophanous , K. A. , Kingsman , S. M. , and Mazarakis , N. D. ( 2004 ).
Transduction patterns of pseudotyped lentiviral vectors in the nervous
system . Mol. Ther. 9 , 101 – 111 .
Xu , F. , Ding , E. , Migone , F. , Serra , D. , Schneider , A. , Chen , Y. T. , and
Amalfitano , A. ( 2005 ). Glycogen storage in multiple muscles of old
GSD-II mice can be rapidly cleared after a single intravenous injection
with a modified adenoviral vector expressing hGAA . J. Gene
Med. 7 , 171 – 178 .
Yang , Y. , Jooss , K. U. , Su , Q. , Ertl , H. C. , and Wilson , J. M. ( 1996 ).
Immune responses to viral antigens versus transgene product in the
elimination of recombinant adenovirus-infected hepatocytes in vivo .
Gene Ther. 3 , 137 – 144 .
Yeager , A. M. , Brennan , S. , Tiffany , C. , Moser , H. W. , and Santos , G. W.
( 1984 ). Prolonged survival and remyelination after hematopoietic cell
transplantation in the twitcher mouse . Science 225 , 1052 – 1054 .